Product Overview
Ataluren | T1805 | TargetMol Chemicals
CAS: 775304-57-9
Smiles: OC(=O)c1cccc(c1)-c1noc(n1)-c1ccccc1F
Formula: C15H9FN2O3
Pathway: Autophagy|||Membrane transporter/Ion channel
Target: CFTR|||Autophagy
Receptor: N/A
Bioactivity: Ataluren is a novel, orally administered drug that targets nonsense mutations. Ataluren is approved for use by the European Medicines Agency to treat Duchenne Muscular Dystrophy in patients aged 5 years and older who are able to walk.
Molecular Weight: 284, 246